#maladies rares

| | Radar

EU orphan drug regulations haven’t “failed” but reforms needed, says European rare disease advocacy group

Two parents hold their child, who has spinal muscular atrophy 1. Source: EURORDIS - Rare Diseases Europe.

Last week, a report published in The BMJ slammed European drug regulations for allowing biopharmaceuticals to reap "billions" in profits on new drugs for rare diseases, but failing to incentivize sufficient R&D into new cures and treatments. A leading patient advocacy group, however, says that while the regulations may be in need of reform, they have helped advance treatments for many debilitating and deadly rare diseases.

Heidi.news sur Telegram, chaque fin de journée, recevez les articles les plus importants.


Recevez chaque matin un résumé de l'actualité envoyé d'une ville différente du monde.